RG7800 (tetrahydrochloride)

MedChem Express

RG7800 (tetrahydrochloride)

10

Research Use Only

99.61

C24H32Cl4N6O

562.36

RG7800 hydrochloride is an orally active SMN2 splicing modulator, with EC 1.5x s of 23 nM and 87 nM for SMN2 splicing and SMN protein ; RG7800 hydrochloride has the potential to treat spinal muscular atrophy.

CC1=CC(C2CCN(C)CC2)=CN3C1=NC(C4=NN(C=C(C)N=C5CC)C5=C4)=CC3=O.[H]Cl.[H]Cl.[H]Cl.[H]Cl

2°C to 8°C

12352200